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Kearns-Sayre Syndrome - 6 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Effect Of The System In The Enriched Fat Metabolism Of The Child Reached Mitochondrial Cytopathy Condición: Mitochondrial Cytopathies Disorders Fecha: 2015-03-02 Intervenciones:
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Completed |
Nombre del estudio: Nutritional Assessment in Mitochondrial Cytopathy Condición:
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Recruiting |
Nombre del estudio: Inherited Retinal Degenerative Disease Registry Condición:
Fecha: 2015-04-03 |
Completed |
Nombre del estudio: Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease Condición: Inherited Mitochondrial Disease, Including Leigh Syndrome Fecha: 2013-12-17 Intervenciones: Drug: Cysteamine Bitartrate Cysteamine Bitartrate Delayed-release Capsules |
Completed |
Nombre del estudio: A Long-Term Extension Study of RP103-MITO-001 (NCT02023866) to Assess RP103 in Children With Inherited Mitochondrial Disease Condición: Mitochondrial Diseases Fecha: 2015-06-10 Intervenciones: Drug: Cysteamine Bitartrate Delayed-release Capsules Treatment with experimental drug as detailed in arm |
Recruiting |
Nombre del estudio: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) Condición:
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