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Leigh Disease - 10 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome Condición: Leigh Syndrome Fecha: 2012-11-01 Intervenciones:
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Enrolling by invitation |
Nombre del estudio: Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome Condición: Leigh Syndrome Fecha: 2014-08-21 Intervenciones: Drug: EPI-743 EPI-743 is a quinone oxidation product of alpha tocotrienol |
Recruiting |
Nombre del estudio: The Leigh Syndrome Registry Condición:
Fecha: 2017-04-28 |
Completed |
Nombre del estudio: Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease Condición: Inherited Mitochondrial Disease, Including Leigh Syndrome Fecha: 2013-12-17 Intervenciones: Drug: Cysteamine Bitartrate Cysteamine Bitartrate Delayed-release Capsules |
Completed |
Nombre del estudio: A Dose-escalating Clinical Trial With KH176 Condición:
Intervenciones: |
Enrolling by invitation |
Nombre del estudio: Tissue Sample Study for Mitochondrial Disorders Condición:
Fecha: 2012-08-31 |
Recruiting |
Nombre del estudio: Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford Condición:
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Active, not recruiting |
Nombre del estudio: EPI-743 for Mitochondrial Respiratory Chain Diseases Condición: Mitochondrial Diseases Fecha: 2011-06-07 Intervenciones: Drug: EPI-743 EPI-743 is administered as a dose escalation from 50 mg bid to 100 mg tid |
Completed |
Nombre del estudio: A Long-Term Extension Study of RP103-MITO-001 (NCT02023866) to Assess RP103 in Children With Inherited Mitochondrial Disease Condición: Mitochondrial Diseases Fecha: 2015-06-10 Intervenciones: Drug: Cysteamine Bitartrate Delayed-release Capsules Treatment with experimental drug as detailed in arm |
Recruiting |
Nombre del estudio: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) Condición:
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