Lysosomal Storage Diseases - 50 Studies Found
Recruiting |
: Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children :
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Not yet recruiting |
: Diet and Exercise in Pompe Disease :
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Terminated |
: Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I :
: Drug: laronidase 0.58 mg/ml solution for intravenous injection, dose 1.74 mg intrathecally once per mont |
Active, not recruiting |
: Characterization of the Patient Population With Galactosialidosis : Galactosialidosis : 2011-08-11 |
Completed |
: Magnetic Stimulation of the Human Nervous System :
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