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Mucopolysaccharidosis II - 30 Studies Found

Estado Estudiar
Active, not recruiting Nombre del estudio: Extension of HGT-HIT-045 Evaluating Long-Term Safety and Clinical Outcomes of Idursulfase (IT)in Conjunction With Elaprase in Pediatric Patients With Hunter Syndrome and Cognitive Impairment
Condición: Hunter Syndrome
Fecha: 2011-12-15
Intervenciones: Drug: Idursulfase-IT Idursulfase-IT administered once monthly at the dose used in study HGT-HIT-045 via
Completed Nombre del estudio: Safety and Efficacy of Hunterase
Condición: Hunter Syndrome
Fecha: 2012-07-16
Intervenciones: Biological: Hunterase once weekly, 0.5mg/kg IV infusion
Completed Nombre del estudio: Observational Study to Evaluate Neurodevelopmental Status in Pediatric Patients With Hunter Syndrome (MPS II)
Condición:
  • Mucopolysaccharidosis (MPS)
  • Hunter Syndrome

Fecha: 2013-03-12
Active, not recruiting Nombre del estudio: Extension of Study HGT-SAN-055 Evaluating Administration of rhHNS in Patients With Sanfilippo Syndrome Type A (MPS IIIA)
Condición: Sanfilippo Syndrome
Fecha: 2011-02-16
Intervenciones:
  • Biological: rhHNS-10 mg Once p
Completed Nombre del estudio: A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)
Condición: Sanfilippo Syndrome Type A
Fecha: 2010-01-11
Intervenciones: Other: assessment Physical, developmental, neurological, behavioral, and neurocognitive assessments
Completed Nombre del estudio: Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)
Condición: Sanfilippo Syndrome Type B
Fecha: 2012-01-10
Completed Nombre del estudio: Safety, Tolerability, Ascending Dose and Dose Frequency Study of rhHNS Via an IDDD in MPS IIIA Patients
Condición: Sanfilippo Syndrome Type A (MPS IIIA)
Fecha: 2010-06-24
Intervenciones:
  • Biological: Recombinant human heparan N-sulfatase

Active, not recruiting Nombre del estudio: A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously
Condición:
  • Mucopolysaccharidosis III, Type B (MPS IIIB)
  • Sanfilippo B

    • Fecha: 2015-10-21
    Intervenciones: Drug: SBC-103
Completed Nombre del estudio: Randomized, Controlled, Open-label, Multicenter, Safety and Efficacy Study of rhHNS Administration Via an IDDD in Pediatric Patients With Early Stage MPS IIIA Disease
Condición: Sanfilippo Syndrome
Fecha: 2014-02-10
Intervenciones: Drug: Recombinant human heparan N-sulfatase [rhHNS] Recombinant human heparan N-sulfatase [rhHNS]
Completed Nombre del estudio: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB
Condición: MPS IIIB (Sanfilippo Syndrome)
Fecha: 2014-11-03
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