Search for Clinical Trial Results
Niemann-Pick Disease Type A - 12 Studies Found
| Status | Study |
| Completed |
Study Name: Study of VTS-270 (2-hydroxypropyl-β-cyclodextrin) to Treat Niemann-Pick Type C1 (NPC1) Disease Condition: Niemann-Pick Disease, Type C Date: 2015-08-18 Interventions:
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| Completed |
Study Name: PET Scan of Brain Metabolism in Relation to Age and Disease Condition:
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