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Gaucher Disease Type 3 - 2 Studies Found
| Estado | Estudiar |
| Completed |
Nombre del estudio: Efficacy and Safety Study of Velaglucerase Alfa in Children and Adolescents With Type 3 Gaucher Disease Condición: Gaucher Disease, Type 3 Fecha: 2012-09-10 Intervenciones: Biological: velaglucerase alfa lyophilized powder, intravenous infusion, units, Every other week (EOW) |
| Completed |
Nombre del estudio: Convection-Enhanced Delivery of Glucocerebrosidase to Treat Type 2 Gaucher Disease Condición: Type 2 Gaucher Disease Fecha: 2005-10-26 |