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Limb-girdle Muscular Dystrophy Type 2I - 4 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Muscle MRI in Becker Muscular Dystrophy and in Limb-girdle Muscular Dystrophy Type 2I Condición:
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Recruiting |
Nombre del estudio: A Trial of PF-06252616 in Ambulatory Participants With LGMD2I Condición: LGMD2I Fecha: 2016-07-12 Intervenciones: Drug: PF 06252616 |
Recruiting |
Nombre del estudio: Congenital Muscle Disease Study of Patient and Family Reported Medical Information Condición:
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RECRUITING |
Nombre del estudio: Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I) Condición: Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I) Fecha: 2024-05-18 Intervenciones: The BBP-418 drug product is provided as Granules for Oral solution consisting of BBP-418 drug substance and silicon dioxide in a multilaminate sachet |