Mucopolysaccharidosis Type I - 5 Studies Found

Enrolling by invitation : Immunodeficiency in Cartilage-hair Hypoplasia: Sub-project on Safety of Vaccination Against Chickenpox
:
: 2025-08-31
Recruiting : Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome
:
: 2025-08-31
Active, not recruiting : Study of Intrathecal Idursulfase-IT Administered in Conjunction With Elaprase® in Pediatric Patients With Hunter Syndrome and Early Cognitive Impairment
:
: 2025-08-31
Enrolling by invitation : Ultrasound Findings of Finger, Wrist and Knee Joints in Mucopolysaccharidosis
:
  • MPS I
  • MPS IV

: 2013-08-13
Completed : Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)
: Mucopolysaccharidosis Type IIIA
: 2025-08-31
: intravenous repeating dose