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Mucopolysaccharidosis Type IIIB - 11 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: A Treatment Study of Mucopolysaccharidosis Type IIIB Condición:
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Completed |
Nombre del estudio: Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B) Condición: Sanfilippo Syndrome Type B Fecha: 2012-01-10 |
Recruiting |
Nombre del estudio: A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB) Condición:
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Completed |
Nombre del estudio: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB Condición: MPS IIIB (Sanfilippo Syndrome) Fecha: 2014-11-03 |
Active, not recruiting |
Nombre del estudio: Natural History Study to Characterise the Course of Disease Progression in Patients With Mucopolysaccharidosis Type IIIB Condición: MPS IIIB (Sanfilippo B Syndrome) Fecha: 2014-11-03 |
Active, not recruiting |
Nombre del estudio: Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in MPS IIIB Condición: Mucopolysaccharidosis IIIB Fecha: 2014-12-15 Intervenciones: Drug: SBC-103 Other Name: recombinant human alpha-N-acetylglucosaminidase (rhNAGLU) |
Completed |
Nombre del estudio: Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging Condición: MPS IIIB (Sanfilippo B Syndrome) Fecha: 2014-03-12 |
Active, not recruiting |
Nombre del estudio: A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously Condición:
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Completed |
Nombre del estudio: Neurobehavioral Phenotypes in MPS III Condición:
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