Niemann-Pick Disease, Type C - 1 Studies Found
| COMPLETED | 
                                    : Arimoclomol Prospective Study in Participants Diagnosed With Niemann-Pick Disease Type C : Niemann-Pick Disease, Type C : 2025-11-04  | 
                                
                | COMPLETED | 
                                    : Arimoclomol Prospective Study in Participants Diagnosed With Niemann-Pick Disease Type C : Niemann-Pick Disease, Type C : 2025-11-04  |