Buscar resultados de ensayos clínicos
Primary Fanconi Syndrome - 25 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Evaluation of Fanconi Syndrome and Cystinosis Condición:
Fecha: 1999-10-18 |
Completed |
Nombre del estudio: Fanconi Syndrome Due to ARVs in HIV-Infected Persons Condición:
Fecha: 2011-09-09 Intervenciones: Drug: Cysteamine bitartrate 500 mg total, single dose taken orally on visits 2, 3 & 4 which must occ |
Completed |
Nombre del estudio: Phase 3 Study of Cysteamine Bitartrate Delayed-release (RP103) Compared to Cystagon® in Patients With Cystinosis Condición: Cystinosis Fecha: 2009-10-22 Intervenciones:
|
Completed |
Nombre del estudio: Pilot Study of Safety, Tolerability, Pharmacokinetics/Pharmacodynamics of RP103 Compared to Cystagon® in Patients With Cystinosis Condición: Cystinosis Fecha: 2009-03-27 Intervenciones:
|
Recruiting |
Nombre del estudio: Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A Condición: Fanconi Anemia Fecha: 2017-04-26 Intervenciones:
|
Recruiting |
Nombre del estudio: Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1 Condición: Fanconi Anemia Fecha: 2016-09-06 Intervenciones:
|
Recruiting |
Nombre del estudio: Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and Plerixafor Condición: Fanconi Anemia Fecha: 2016-02-05 Intervenciones:
|